Pastores et al outlined therapeutic goals for a child with Gaucher Disease. Some of the goals involve growth and skeletal bone health.


Goals for growth and development:

(1) To achieve an acceptable height, ideally normal for the population.

(2) To experience the normal onset of puberty.


Goals for bone health:

(1) To improve bone mineral density, ideally being normal.

(2) To reduce or eliminate bone pain.

(3) To prevent bone crises.

(4) To prevent osteonecrosis and subchondral joint collapse.


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